it s a game changer. it is absolutely changed the face of sma. this is when he was seven weeks old in hospital. he had just been resuscitated by his dad. later diagnosed with severe spinal muscular atrophy. the vectors deliver new working copies of sma genes to the motor neuron cells. this new, one off drug contains a replica of the missing gene, halting the progression of the disease, helping babies breathe without a ventilator and even crawl and walk. he shouldn t really feel anything. he s got a cannula in, which is a little bit of plastic into his vein. and the drug just goes through that over an hour. injune, five month old arthur became the first baby to receive this revolutionary treatment on the nhs. now edward is one of a handful of babies being treated for the first time at the children s
administered at the children s hospital in sheffield. without medical intervention, he wouldn t live to his second birthday. his parents have been scared he wouldn t get this amazing chance of life. yay! we re just so relieved, excited, scared, apprehensive, nervous absolutely, completely petrified. it s a game changer. it has absolutely changed the face of sma. this is when he was seven weeks old in hospital. he had just been resuscitated by his dad. later diagnosed with severe spinal muscular atrophy. the vectors deliver new working copies of sma genes to the motor neuron cells. this new, one off drug contains a replica of the missing gene, halting the progression of the disease, helping babies breathe without a ventilator and even crawl and walk. he shouldn t really feel anything. he s got a cannula in, which is a little bit of plastic into his vein. and the drug just goes
£1.79 million and is administered at the children s hospital in sheffield. without medical intervention, he would not live until his second birthday point of his parents have been scared he would not get the amazing chance of life. we would not get the amazing chance of life. ~ ., , would not get the amazing chance of life. 2 . , ,., ., life. we are ust so relieved and excited, life. we are just so relieved and excited, scared life. we are just so relieved and excited, scared and life. we are just so relieved and i excited, scared and apprehensive. nervous. absolutely completely petrified! it is a game changer, it is absolutely changed the face of sma. , ., , ., , , sma. this was when he was seven weeks old in sma. this was when he was seven weeks old in hospital sma. this was when he was seven weeks old in hospital having i sma. this was when he was seven weeks old in hospital having just l weeks old in hospital having just been resuscitated by his dad put it was later diagno
got a cannula in which is a bit of plastic into his vein. got a cannula in which is a bit of plastic into his vein. and - got a cannula in which is a bit of plastic into his vein. and the i got a cannula in which is a bit of. plastic into his vein. and the drug goes plastic into his vein. and the drug goes through plastic into his vein. and the drug goes through that plastic into his vein. and the drug goes through that over plastic into his vein. and the drug goes through that over an - plastic into his vein. and the drug goes through that over an hour. l plastic into his vein. and the drugl goes through that over an hour. in june, goes through that over an hour. june, five months aso became goes through that over an hounm june, five months aso became the first baby to receive the revolutionary treatment on the nhs. now edward is one of a handful of babies being treated for the first time at the children s hospital in sheffield. . ~ time at the children s hospital in sheffi