administered at the children's hospital in sheffield. without medical intervention, he wouldn't live to his second birthday. his parents have been scared he wouldn't get this amazing chance of life. yay! we're just so relieved, excited, scared, apprehensive, nervous — absolutely, completely petrified. it's a game changer. it has absolutely changed the face of sma. this is when he was seven weeks old in hospital. he had just been resuscitated by his dad. later diagnosed with severe spinal muscular atrophy. the vectors deliver new working copies of sma genes to the motor neuron cells. this new, one—off drug contains a replica of the missing gene, halting the progression of the disease, helping babies breathe without a ventilator and even crawl and walk. he shouldn't really feel anything. he's got a cannula in, which is a little bit of plastic into his vein. and the drug just goes