debbie tubby reports. edward just needs this one single infusion to transform his life. it s a new gene therapy called zolgensma, costing £1.79 million, administered at the children s hospital in sheffield. without medical intervention, he wouldn t live to his second birthday. his parents have been scared he wouldn t get this amazing chance of life. yay! we re just so relieved, excited, scared, apprehensive, nervous absolutely, completely petrified. it s a game changer. it has absolutely changed the face of sma. this is when he was seven weeks old in hospital. he had just been resuscitated by his dad. later diagnosed with severe spinal muscular atrophy. the vectors deliver new working copies of sma genes to the motor neuron cells. this new, one off drug contains a replica of the missing gene, halting the progression of the disease, helping babies breathe without a ventilator and even crawl and walk.
flexible working. chris, really good to talk to you- flexible working. chris, really good to talk to you. i am glad to see you are takin: to talk to you. i am glad to see you are taking advantage to talk to you. i am glad to see you are taking advantage of to talk to you. i am glad to see you are taking advantage of that - to talk to you. i am glad to see you are taking advantage of that you i are taking advantage of that you would are taking advantage of that you would not be loving the story. they will not would not be loving the story. they will not let would not be loving the story. they will not let me! i have asked them. a baby with a fatal condition has received the world s most expensive drug after a campaign by his parents. 11 month old edward, from colchester, has severe spinal muscular atrophy which means he lacks a protein vital for muscle development. he received a new gene therapy which costs nearly 1.8 million pounds, at sheffield children s hospital. debbie
of summer. a very ominous indicator of what twitter might bring. what winter might bring. a baby with a fatal condition has received the world s most expensive drug after a campaign by his parents. 11 month old edward, from colchester, has severe spinal muscular atrophy, which means he lacks a protein vital for muscle development. he received a new gene therapy, which costs nearly £1.8 million at sheffield children s hospital. debbie tubby from bbc look east reports. edward just needs this one single infusion to transfer his life. it s a new gene therapy called zolgensma, costing £1.79 million, administered at the children s hospital in sheffield. without medical intervention, he wouldn t live to his second birthday. his parents have been scared he wouldn t get this amazing chance of life. yay! we re just so relieved, excited, scared, apprehensive, nervous absolutely, completely petrified.
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small businesses hit hard. how many had to shut their doors. here with more is diane macedo. the recession claimed more than 170,000 small businesses in the u.s. between 2008 and 2010. the report shows a number of small businesses operating within the country s met poll can and micro politan areas dropped to 6.79 million in 2010 from 6.96 in 2008. self-employed americans took a 12 point dive since neovember. 2007. one month when it officially hit to june 2009 more businesses shut down in 2009 than did in 2007. official statistics aren t available for 2011 or 2012 yet but those numbers are expected to pick back up. that is due to people who are laid off starting small businesses because they had no