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New Advancement Toward The First Primary Endpoint Qualification Of A Digital Endpoint For Duchenne

Current methods for assessing ambulatory function in patients with Duchenne muscular dystrophy do not fully reflect how they experience DMD in their. ....

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New Four-Year Data for Genentech's Evrysdi Reinforce Long-Term Efficacy and Safety Profile in Some of the Most Severely Affected People With Types 2 and 3 Spinal Muscular Atrophy (SMA) Seite 1

20.03.2023 - Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), today announced new long-term data for Evrysdi (risdiplam) in a broad range of people aged 2-25 years with spinal muscular atrophy (SMA) from the pivotal SUNFISH study. Data . Seite 1 ....

Laurent Servais , Levi Garraway , Muscular Dystrophy Association , Roche Group , Global Product Development , Oxford Neuromuscular Centre , Scientific Conference , Paediatric Neuromuscular Diseases , Motor Function , Revised Upper Limb Module , Global Product , Roche Holding ,

F. Hoffmann-La Roche Ltd: New four year data for Roche's Evrysdi reinforce long-term efficacy and safety profile in some of the most severely affected people with types 2 and 3 spinal muscular atrophy (SMA)

Data from pivotal SUNFISH study showed increases in motor function observed during the first year were maintained through the fourth year, while the overall rate of adverse events continued to decrease ....

United States , United Kingdom , Levi Garraway , Sabine Borngr , Gerard Tobin , Bruno Eschli , Laurent Servais , Birgit Masjost , Loren Kalm , Nathalie Altermatt , Muscular Dystrophy Association , Society For Medicines Research , Toddler Development , British Pharmacological Society , Drug Administration , Head Of Global Product Development , Oxford Neuromuscular Centre , European Medicines Agency , Roche Group , Office Of Orphan Products Development , Roche Group Media Relations , Scientific Conference , Paediatric Neuromuscular Diseases , Motor Function Measure , Revised Upper Limb Module , Chief Medical Officer ,

Solid Biosciences Presents New SGT-001 IGNITE DMD Study Results at World Muscle Society 2022 Congress Demonstrating Improvements in Ambulatory Function

Solid Biosciences Presents New SGT-001 IGNITE DMD Study Results at World Muscle Society 2022 Congress Demonstrating Improvements in Ambulatory Function
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Solid Biosciences (SLDB) Presents New SGT-001 IGNITE DMD Study Results

Solid Biosciences (SLDB) Presents New SGT-001 IGNITE DMD Study Results
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