Affinity Duchenne News Today : Breaking News, Live Updates & Top Stories | Vimarsana

Stay updated with breaking news from Affinity duchenne. Get real-time updates on events, politics, business, and more. Visit us for reliable news and exclusive interviews.

Top News In Affinity Duchenne Today - Breaking & Trending Today

Phase 1/2 Findings Highlight RGX-202's Safety, Impact on Key Duchenne Biomarkers

RGX-202, a gene therapy for Duchenne muscular dystrophy, was well tolerated with no therapy-related serious adverse effects in 3 patients who received the level 1 dosage. ....

United States , Aravindhan Veerapandiyan , Olivier Danos , Manufacturing Innovation Center , World Muscle Society , International Congress , Arkansas Children , North Star Ambulatory Assessment , Innovation Center , Rgx 202 , Duchenne Muscular Dystrophy , Level 1 Dosage , Serum Creatine Kinase , Affinity Duchenne ,

FDA grants fast track designation for novel Duchenne muscular dystrophy gene therapy

Regenxbio Inc. announced that the FDA has granted fast track designation for RGX-202, a one-time gene therapy for treatment of Duchenne muscular dystrophy.According to a release from the company, the FDA previously granted orphan drug designation and rare pediatric disease designation for RGX-202, which is designed to support delivery and expression of genes in heart and skeletal muscle using the ....

United States , Heather Biele , Regenxbio Inc , Adobe Stock , Affinity Beyond , Affinity Duchenne ,