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FDA: More Data Needed to Support Arimoclomol in Niemann-Pick Disease Type C

FDA: More Data Needed to Support Arimoclomol in Niemann-Pick Disease Type C
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Christophe Bourdon , Drug Administration , Complete Response Letter , New Drug Application , Severity Scale , கிறிஸ்டோஃப் பெர்டோன் , முழுமை பதில் கடிதம் , புதியது மருந்து விண்ணப்பம் , தீவிரம் அளவு ,

Orphazyme presents 36-month data supporting durable response to arimoclomol during Parseghian ...


Press release content from Globe Newswire. The AP news staff was not involved in its creation.
Orphazyme presents 36-month data supporting durable response to arimoclomol during Parseghian .
ORPHAZYME A/SJune 28, 2021 GMT
Orphazyme A/S
Company Registration No. 32266355
Copenhagen – June 28, 2021 – Orphazyme A/S (ORPHA.CO; ORPH), a late-stage biopharmaceutical company, today announced 24-month interim results of an open-label extension (OLE) trial, providing efficacy and safety data for its investigational treatment arimoclomol in Niemann-Pick disease type C (NPC) for up to 36 months. The data are featured in a presentation as part of the Parseghian Scientific Conference for Niemann-Pick disease type C Research. ....

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