lena was treated as a baby with zolgensma the drug came too late for amelia. lena is our little miracle. we knew that if we give lena the drug before any symptoms, it will be the best effect. that s why the pre screening, it s so important. this is clearly a remarkable family. amelia can t get to school half the time because of chest infections and hospital appointments, yet this gcse student is in all the top sets at school. do you think that you have to try harder and work harder than anybody else? oh, yeah, definitely. definitely. this week alone i m missing a whole day of school. so what will you have to do to catch up? i will have to catch up over the weekend. but when i ask her about her sister, lena, this strong, determined
this is three year old lena s preferred mode of travel whizzing by in the lap of her 16 year old sister, amelia. they both have sma although a different type from edward s. lena was treated as a baby with zolgensma the drug came too late for amelia. lena is our little miracle. we knew that if we give lena the drug before any symptoms, it will be the best effect. that s why the pre screening, it s so important. this is clearly a remarkable family. amelia can t get to school half the time because of chest infections and hospital appointments, yet this gcse student is in all the top sets at school. do you think that you have to try harder and work harder than anybody else? oh, yeah, definitely. definitely.
and so it makes you appreciate every single little thing every tantrum i appreciate because he can. he s got the strength to be a naughty boy, you know? and it s all those things that ijust didn t even think he would ever be able to do. row, row, row. spinal muscular atrophy can be detected in newborns using a simple heel prick blood test. the condition affects one in 10,000 babies. great 0rmond street is calling for all newborns to be given the test. this is three year old lena s preferred mode of travel whizzing by in the lap of her 16 year old sister, amelia. they both have sma although a different type from edward s. lena was treated as a baby with zolgensma the drug came too late for amelia. lena is our little miracle. we knew that if we give lena the drug before any symptoms, it will be the best
this is three year old lena s preferred mode of travel whizzing by in the lap of her 16 year old sister, amelia. they both have sma although a different type from edward s. lena was treated as a baby with zolgensma the drug came too late for amelia. lena is our little miracle. we knew that if we give lena the drug before any symptoms, it will be the best effect. that s why the pre screening, it s so important. i think it s amazing, i wasn t able to walk i think it s amazing, i wasn t able to walk from the age of one and a half to walk from the age of one and a half i to walk from the age of one and a half. i wasn t able to run, i wasn t able half. iwasn t able to run, i wasn t able to half. i wasn t able to run, i wasn t able to even half. i wasn t able to run, i wasn t able to even crawl. so, yeah, it s quite able to even crawl. so, yeah, it s
lena was treated as a baby with zolgensma the drug came too late for amelia. lena is our little miracle. we knew that if we give lena the drug before any symptoms, it will be the best effect. that s why the pre screening, it s so important. this is clearly a remarkable family. amelia can t get to school half the time because of chest infections and hospital appointments, yet this gcse student is in all the top sets at school. do you think that you have to try harder and work harder than anybody else? oh, yeah, definitely. definitely. this week alone i m missing a whole day of school. so what will you have to do to catch up? i will have to catch up over the weekend. but when i ask her about her sister, lena, this strong, determined