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Azafaros announces completion of 12-week Phase 2 RAINBOW study evaluating lead asset nizubaglustat in rare disease patients

Azafaros announces completion of 12-week Phase 2 RAINBOW study evaluating lead asset nizubaglustat in rare disease patients
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United statesUnited kingdomAsahi kasei pharmaAmber fennellAshley tappChris freitagRoberto giuglianiPorto alegreLeiden universityDrug administrationEuropean medicines agencyGenetics clinical research groupHealthcare products regulatory agencyMedical genetics clinical research groupHospital de clinicas porto alegreLead principal investigator

Azafaros to present data from PRONTO study in patients with GM1 and GM2 gangliosidoses at the 20th annual WORLDSymposium™

Azafaros to present data from PRONTO study in patients with GM1 and GM2 gangliosidoses at the 20th annual WORLDSymposium™
tmcnet.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from tmcnet.com Daily Mail and Mail on Sunday newspapers.

United statesSan diegoUnited kingdomAsahi kasei pharmaChristian freitagLeiden universityHealthcare products regulatory agencyEuropean medicines agencyDrug administrationMolecular geneticsLysosomal storageChief medical officerStates foodPediatric disease designationsDrug designationsTay sachs diseases