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Dyne Therapeutics Announces New Clinical Data from ACHIEVE Trial of DYNE-101 in DM1 and DELIVER Trial of DYNE-251 in DMD Demonstrating Compelling Impact on Key Disease Biomarkers and Improvement in Multiple Functional Endpoints

- In Phase 1/2 ACHIEVE Trial, DYNE-101 Demonstrated Dose Dependent 27% Mean Splicing Correction Across All Patients in the 5.4 mg/kg Cohort at 3 Months - - DYNE-101 Showed Improvement in Myotonia,. ....

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Dyne Therapeutics Announces New Clinical Data from ACHIEVE

- In Phase 1/2 ACHIEVE Trial, DYNE-101 Demonstrated Dose Dependent 27% Mean Splicing Correction Across All Patients in the 5.4 mg/kg Cohort at 3 Months - . ....

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PepGen Reports First Quarter 2024 Financial Results and Recent Corporate Highlights

PepGen Reports First Quarter 2024 Financial Results and Recent Corporate Highlights
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Avidity Biosciences Receives FDA Breakthrough Therapy Designation for Delpacibart Etedesiran (AOC 1001) for Treatment of Myotonic Dystrophy Type 1

Avidity Biosciences Receives FDA Breakthrough Therapy Designation for Delpacibart Etedesiran (AOC 1001) for Treatment of Myotonic Dystrophy Type 1
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Myotonic Dystrophy Pipeline Assessment 2024 | In-Depth Insights Into The Emerging Drugs, Latest FDA Approvals, Clinical Trials, Ter, Key Companies

Myotonic Dystrophy Pipeline Assessment 2024 | In-Depth Insights Into The Emerging Drugs, Latest FDA Approvals, Clinical Trials, Ter, Key Companies
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