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PTC Therapeutics Announces Validation of Sepiapterin European MAA

- Review of European marketing application for PKU now initiated - WARREN, N.J., May 28, 2024 /PRNewswire/ PTC Therapeutics, Inc. announced today that the sepiapterin MAA for PKU has been.

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PTC Therapeutics Announces European Commission Returns Translarna™ Opinion to CHMP For Re-evaluation

- European Commission decides against adoption of negative opinion - - Translarna authorization remains active in Europe - - 2024 revenue guidance paused - WARREN, N.J., May 20, 2024 /PRNewswire/ .

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PTC Therapeutics Announces FDA Acceptance and Priority Review of the BLA for Upstaza™

PTC Therapeutics Announces FDA Acceptance and Priority Review of the BLA for Upstaza™
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