Brain of little 'angel' donated for research after 3yo dies from rare Angelman Syndrome abc.net.au - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from abc.net.au Daily Mail and Mail on Sunday newspapers.
The Foundation for Angelman Syndrome Therapeutics (FAST) announced today that the non-profit organization has entered into an exclusive global collaborative research and development agreement with the University of Pennsylvania to develop an investigational adeno-associated virus (AAV) gene therapy for Angelman syndrome (AS).
Couragene co-founders awarded $40M NIH grant njbiz.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from njbiz.com Daily Mail and Mail on Sunday newspapers.
The National Institute of Health announced a $40 million grant for researchers to develop a CRISPR-mediated platform for genome editing in the brain and to treat genetic disorders.