STEALTH BIOTHERAPEUTICS' BARTH SYNDROME NDA RECEIVES PRIORITY REVIEW DESIGNATION prnewswire.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from prnewswire.com Daily Mail and Mail on Sunday newspapers.
Financings of Public Rare Disease Drug Developers Soar & More - This Week in RARE Daily globalgenes.org - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from globalgenes.org Daily Mail and Mail on Sunday newspapers.
The Upshot: The NY Islanders find the win column again dismantling the Jets eyesonisles.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from eyesonisles.com Daily Mail and Mail on Sunday newspapers.
Barth Syndrome is a rare congenital genetic disorder caused by an abnormality in the X chromosome. Find out about the symptoms, causes and treatment of the condition.
There are about 300 people worldwide living with Barth Syndrome, and 8-year-old Deacon Dague in Hollywood is one of them. His family hopes to raise more awareness so that there will be a cure one day.