Study Validates First Disease-Specific PRO Instrument for Pa

Congenital thrombotic thrombocytopenic purpura (TTP), an ultra-rare disease, can significantly impact quality of life, but clinicians have previously lacked a disease-specific way to track experiences via patient-reported outcomes (PROs).

Related Keywords

United States , American , , American Journal , Ultra Rare Disease , Patient Reported Outcomes , Cttp Peq , Adamts13 , Quality Of Life , Hrqol ,