Study suggests gene therapy as promising cure
ANI
11 May 2021, 23:56 GMT+10
California [US], May 11 (ANI): Researchers have developed a gene therapy that successfully treated 48 out of 50 children with a form of severe combined immunodeficiency that leaves them without an immune system.
The study led by an international team of researchers at Great Ormond Street Hospital (GOSH), and the University of California, Los Angeles (UCLA) - was published in the New England Journal of Medicine.
Severe combined immunodeficiency due to adenosine deaminase deficiency, also known as ADA-SCID, is a rare, life-threatening disease that prevents children from living a normal life. It is caused by mutations in the gene that creates the enzyme adenosine deaminase, which is essential to a functioning immune system.
Experimental gene therapy successfully treats children born without an immune system
An experimental form of gene therapy developed by a team of researchers from UCLA and Great Ormond Street Hospital in London has successfully treated 48 of 50 children born with a rare and deadly inherited disorder that leaves them without an immune system.
Severe combined immunodeficiency due to adenosine deaminase deficiency, or ADA-SCID, is caused by mutations in the ADA gene that creates the enzyme adenosine deaminase, which is essential to a functioning immune system. For children with the condition, even day-to-day activities like going to school or playing with friends can lead to dangerous, life-threatening infections. If untreated, ADA-SCID can be fatal within the first two years of life.
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Booth, Nash Ensemble, Wigmore Hall online review - contemporary music programme lacks diversity | reviews, news & interviews Booth, Nash Ensemble, Wigmore Hall online review - contemporary music programme lacks diversity
Booth, Nash Ensemble, Wigmore Hall online review - contemporary music programme lacks diversity
Excellent playing and singing can’t disguise the absence of variety
by Bernard HughesWednesday, 28 April 2021
The Nash Ensemble with soprano Claire Booth
Wigmore Hall does not dish up a great deal of contemporary music, preferring a menu of mainstream chamber music.
Wigmore Hall does not dish up a great deal of contemporary music, preferring a menu of mainstream chamber music. But this programme by the Nash Ensemble offered a different kind of mainstream: within the world of contemporary music this was a middle-of-the-road offering. A roster of composers including Harrison Birtwistle, Simon Holt and Mark-Antony Turnage, all at one time
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