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Gene therapy fails for Danish child treated for Sandhoff disease

Alissa Feldborg, a 3-year-old with an ultra rare genetic disease called Sandhoff, died this month after participating in a gene therapy trial.

United statesFrancis collinsThomas feldborgAlissa feldborgDaria rokinaRobert deutschUmass chanTerence flotteKaren weintraubDrug administrationNational institutes of healthTh chan school of medicineUniversity of massachusettsEaster mondayBaby fitzNational institutes

USA Today reports on first baby in gene therapy clinical trial for Sandhoff, Tay-Sachs diseases

USA Today reports on first baby in gene therapy clinical trial for Sandhoff, Tay-Sachs diseases
umassmed.edu - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from umassmed.edu Daily Mail and Mail on Sunday newspapers.

United statesThomas feldborgTerencer flotteDouglas martinDaria rokinaKaren weintraubHeather gray edwardsMiguel sena estevesSchool of medicineUmass medical schoolAuburn university college of veterinary medicineUmass memorial medical centerUnited states todaySio geneMedical schoolMemorial medical

An experimental gene therapy was little Alissa s only hope Now, instead of certain death, she faces an uncertain future

An experimental gene therapy was little Alissa s only hope. Now, instead of certain death, she faces an uncertain future. Karen Weintraub, USA TODAY © Feldborg family photo Alissa Feldborg BOSTON Thomas Feldborg and Daria Rokina set off nearly every afternoon to explore this city. They leave from their hotel in the Charlestown neighborhood, pushing their baby carriage, some days heading deep into downtown, others choosing a path along the Charles River. Every few minutes, Rokina stops to peek inside and check on 16-month-old Alissa. She gently rubs Alissa s cheek and coos a few soothing words, making sure the little girl is warm enough in her yellow snowsuit and adjusting her sparkly unicorn earmuffs.

United statesUniversity of massachusettsAuburn universityCummings schoolCharles riverThomas feldborgFeldenkrais methodPavan cheruvuDaria rokinaMiguel sena estevesCynthia tifftFlorian eichlerIsaac kohaneDouglas martinMatty wilkinsonJoan horak

Gene therapy offers hope for Danish girl, but uncertainty lies ahead

12:12 pm UTC Apr. 25, 2021 BOSTON Thomas Feldborg and Daria Rokina set off nearly every afternoon to explore this city. They leave from their hotel in the Charlestown neighborhood, pushing their baby carriage, some days heading deep into downtown, others choosing a path along the Charles River. Every few minutes, Rokina stops to peek inside and check on 16-month-old Alissa. She gently rubs Alissa s cheek and coos a few soothing words, making sure the little girl is warm enough in her yellow snowsuit and adjusting her sparkly unicorn earmuffs. Alissa rests better in the outside air. The daily walks allow the couple to relieve some of the stress of not knowing whether their daughter will survive

Charles riverUnited statesUniversity of massachusettsThomas feldborgRobert deutschIsaac kohaneDaria rokinaCynthia tifftDepartment of biomedical informaticsPediatric undiagnosed diseases programDiseases networkNational institutes of healthHarvard medical schoolBefore alissaNational institutesBiomedical informatics

Gene therapy offers hope for Danish girl, but uncertainty lies ahead

Gene therapy offers hope for Danish girl, but uncertainty lies ahead
jsonline.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from jsonline.com Daily Mail and Mail on Sunday newspapers.

Charles riverUnited statesUniversity of massachusettsThomas feldborgRobert deutschIsaac kohaneDaria rokinaCynthia tifftDepartment of biomedical informaticsPediatric undiagnosed diseases programDiseases networkNational institutes of healthHarvard medical schoolBefore alissaNational institutesBiomedical informatics