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Impact of Recombinant Replacement Therapy Detailed in Genetic Clotting Disorder

Adzynma Approved for Congenital Thrombotic Thrombocytopenic Purpura

The FDA has approved Adzynma for prophylactic or on demand enzyme replacement therapy in patients with congenital thrombotic thrombocytopenic purpura.

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FDA Approves Adzynma for Treatment of Congenital Thrombotic Thrombocytopenic Purpura

Adzynma is the first product to be approved for the treatment of the rare blood disorder that has 90% mortality when left untreated.

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Takeda Pharmaceutical (TAK) Announces FDA Approval of ADZYNMA

Takeda Pharmaceutical (TAK) Announces FDA Approval of ADZYNMA
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