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Erik Sontheimer co-leading efforts to develop gene editing toolkit by NIH Somatic Cell Genome Editing Consortium By Jim Fessenden April 07, 2021
Six UMass Medical School scientists are among the members of the National Institutes of Health’s Somatic Cell Genome Editing Consortium to publish a paper in
Nature outlining the program’s goals to accelerate and benchmark the development of safer, more effective methods to edit the genomes of disease-relevant somatic cells in patients. Their research comprising new genome editors, delivery technologies, methods for tracking edited cells in vivo, animal models and human biological systems will be made available as a toolkit that other biomedical researchers can access and apply to an array of disease types and cell tissues as a means of accelerating the clinical development of new therapies for a wide range of illnesses.