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Breakthrough Gene Therapy at Primary Childrenâs Hospital helps little cowboy thrive
A rare, progressive genetic disease thatâs often fatal for infants and toddlers has been stopped its tracks by a groundbreaking gene therapy at Intermountain Primary Childrenâs Hospital.
By: Sponsored Content
and last updated 2021-02-11 10:35:47-05
A rare, progressive genetic disease thatâs often fatal for infants and toddlers has been stopped its tracks by a groundbreaking gene therapy at Intermountain Primary Childrenâs Hospital.
Primary Childrenâs was one of the first in the United States to offer the gene therapy Zolgensma, used to treat spinal muscular atrophy (SMA) in children younger than 2 years.
A little cowboy was saved by a groundbreaking new therapy Author: Jim Mertens Updated: 6:30 PM CST January 8, 2021
SALT LAKE CITY It s amazing Cinch Wright is alive.
The little boy got cutting edge gene therapy that replaced disease-causing genes with healthy ones.
It can knock out a gene that s not working right, or add a new gene to the body to help fight disease. He loves the dog and the horses and the cows, says Alex Wight about his son.
No doubt about it, Cinch Wight is going to be a cowboy just like his dad.
To date, the FDA has approved four types of gene therapy including one that was given approval just in time for Cinch.