A research team led by gene editing pioneer David R. Liu, PhD, has published how it has applied the technology to develop a one-time treatment for spinal muscular atrophy (SMA) that showed effectiveness in cell and mouse models.
Calorie restriction has long been associated with reduced seizures in epilepsy. New research from Boston Children's Hospital helps explain how fasting affects neurons in the brain and could lead the way to new approaches that would avoid the need for fasting or restrictive diets. The findings were published August 30 in the journal Cell Reports.
Cerebral palsy, a non-progressing motor impairment that begins in early childhood, has widely been viewed as the result of oxygen deprivation during birth or other birth-related factors such as prematurity.