European Commission Grants Ocugen Orphan Medicinal Product Designation for Gene Therapy Product Candidate, OCU400, For the Treatment of Both Retinitis Pigmentosa and Leber Congenital Amaurosis
NR2E3), for the treatment of both retinitis pigmentosa (RP) and Leber Congenital amaurosis (LCA).
The prevalence of RP in Europe is estimated at approximately 165,000 patients and the prevalence of LCA in Europe is estimated at approximately 40,000 patients. Globally, the number of people suffering from RP and LCA is estimated to be around 2.0 million and 0.2 million, respectively. We believe the granting of this designation by the European Commission validates the potential of our modifier gene therapy platform to treat many inherited retinal diseases, Chairman of the Board, Chief Executive Officer, and Co-founder of Ocugen.
without all of the information? first in this week s turning point, at 50, this woman did not know how to swim until she got a tough diagnosis that changed everything. when i was younger, for woman of color, swimming was taboo. at the age of 19, i was told that i had retinitis. before i started to swim, i had depression, no motivation. i had high blood pressure and diabetes. i was 319 pounds. a doctor told me i was going to die. so i start swimming. i was petrified. it wasn t as bad as i thought, and i asked my coach, could i do it again. i lost over 100 pounds. i have won over 275 medals at
one of the doctors performing the surgery at kellogg and just finished the fourth. thank you so much for your time. this is an incredible technology. four surgeries, i have to ask, when will we see more? we have scheduled next month in may. we ll see how that goes. this sounds like the technology and i m heard you ve heard it it a million times, the 6 million dollar man, the bionic body part but this is a reality. tell us why it is so successful with these individuals? well, these patients have no other treatment options, they re lost all of their vision from this disease called retinitis and had good vision in childhood and lost vision during the course of their life. there isn t anything else that we can do for them right now. so that s why it s been
bladder or bowel incontinence. so you re going through and he denies fevers or chills. correct. his eye, doesn t have blurred vision double vision. ears, nose, mouth and throat. tell bus about that. he admits to nose pain but has no hearing loss or ringing in the ears. what is the significance of that? the significance of the tinitis, would there be any significant side effects of that, hearing loss or ringing in the ears. so he has no hearing loss or ringing in the ears? he denies both.