The Rare Disease Fund (RDF) is a charity fund, in which the Government matches donations three to one. It is managed by the RDF Committee (RDFC), and oversees fundraising efforts and donor engagement. The expansion of the RDF to cover cell, tissue and gene therapy products and the ability to draw on the principal do
Desperate parents launch S$2 4 million crowdfunding campaign to save baby Lucas from rare genetic disorder theonlinecitizen.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from theonlinecitizen.com Daily Mail and Mail on Sunday newspapers.
It is known as the "world's most expensive medicine", priced at a jaw-dropping $2.4 million per pop. But it's also what three-month-old baby Lucas needs in order to have a chance at life. Lucas was born with a rare genetic disorder known as Spinal Muscular Atrophy Type 1, reported Shin Min Daily News on Saturday (July 8). The neuromuscular disorder.
Zolgensma, used to treat a rare but often fatal genetic disease, has been approved in Singapore. It is an opportunity to rethink how innovative, expensive gene therapies are financed, say doctors Ng Qin Xiang, Chan Hwei Wuen and Jeremy Lim.
Singapore News - When their son started gagging and refusing his food at about eight months old, the first-time parents knew something was amiss. A month later, Baby Shamel was not able to sit up and showed no signs of being able to put weight on his legs. Soon after, he lost the. Read more at www.tnp.sg