comparemela.com

Rapid Mr International News Today : Breaking News, Live Updates & Top Stories | Vimarsana

Antisense oligonucleotide therapeutic approach for Timothy syndrome

Timothy syndrome (TS) is a severe, multisystem disorder characterized by autism, epilepsy, long-QT syndrome and other neuropsychiatric conditions1. TS type 1 (TS1) is caused by a gain-of-function variant in the alternatively spliced and developmentally enriched CACNA1C exon 8A, as opposed to its counterpart exon 8. We previously uncovered several phenotypes in neurons derived from patients with TS1, including delayed channel inactivation, prolonged depolarization-induced calcium rise, impaired interneuron migration, activity-dependent dendrite retraction and an unanticipated persistent expression of exon 8A2–6. We reasoned that switching CACNA1C exon utilization from 8A to 8 would represent a potential therapeutic strategy. Here we developed antisense oligonucleotides (ASOs) to effectively decrease the inclusion of exon 8A in human cells both in vitro and, following transplantation, in vivo. We discovered that the ASO-mediated switch from exon 

Magnetic Resonance Imaging Coils Market in Japan is projected to register a CAGR of nearly 9 5% duri

The Magnetic Resonance Imaging Coils Market revenues were estimated at US$ 8.5 Billion in 2022 and are anticipated to grow at a CAGR of 8.3% from 2023 to 2033, according to a recently published Future Market Insights report. By the end of 2033, the market is expected to reach a valuation of US$ 20.3 Billion.The expa.

Research Report on Magnetic Resonance Imaging Coil Market

© 2025 Vimarsana

vimarsana © 2020. All Rights Reserved.