/PRNewswire/ Neurophth Biotechnology Ltd., a fully-integrated genomic medicines company seeking to improve lives through the curative potential of gene.
First in China! Neurophth announced the first patient has been dosed in G O L D clinical trial for the gene therapy treatment of LHON prnewswire.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from prnewswire.com Daily Mail and Mail on Sunday newspapers.
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HOUSTON and SAN DIEGO, June 1, 2021 /PRNewswire/ Neurophth Biotechnology Ltd., a fully-integrated genetic medicines company developing AAV-mediated gene therapies for the treatment of ocular diseases, and Hopstem Biotechnology, the leading human induced pluripotent stem cell (hiPSC) and neural differentiation technology platform company, today announced a strategic partnership aiming to provide human iPSC-derived cell therapy for ocular diseases.
The partnership leverages Neurophth s experience in global gene/cell therapy drugs development and understanding of ophthalmic diseases to complement Hopstem s expertise in GMP manufacturing and quality assurance of iPSC-derived clinical cell products to provide next-generation ocular treatments. Under the terms of agreement, Hopstem Biotechnology will receive upfront and milestone payments for the development of candidate cell product for agreed retinal degenerative disorder. Neurophth will have th
Neurophth Announces IND Approval by the NMPA for Leber Hereditary Optic Neuropathy Gene Therapy
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WUHAN and SUZHOU, China, April 1, 2021 /PRNewswire/ Neurophth Biotechnology Ltd., a fully-integrated genomic medicines company developing adeno-associated viral (AAV)-delivered gene therapies for the treatment of ocular diseases, recently announced the Center for Drug Evaluation (CDE) of China National Medical Products Administration (NMPA) has approved the Company s Investigational New Drug (IND) application of NR082 (recombinant adeno-associated virus serotype 2 carrying
ND4 gene; rAAV2-
ND4 mutations.
It marks the first AAV2 gene therapy IND application approval in China. Previously, the company announced NR082 has granted orphan drug designation by the US FDA in September 2020