A novel therapy for ataxia telangiectasia that delivers dexamethasone sodium phosphate through red blood cells is both promising and impressive in a new phase 3 trial, experts say.
The vaccine likely kick-started his immune system, according to the doctors, who hope the approach can be used for other patients who have an impaired immune system.
Treatment with the experimental drug donidalorsen cut the number of attacks over 17 weeks by 90% in people with hereditary angioedema, according to the results from a phase 2 trial.
Individuals with primary immunodeficiencies should be screened earlier for GI cancers. This study was published on medRxiv.org as a preprint and has not yet been peer reviewed.
Scientists discover rare genetic condition that attacks kids immune systems – Washington University School of Medicine in St Louis wustl.edu - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from wustl.edu Daily Mail and Mail on Sunday newspapers.