/PRNewswire/ Multi-platinum-selling artist and songwriter Chris Janson will perform at global brain and vision research nonprofit BrightFocus Foundation s.
The State of Gene Therapy
May 4, 2021
Time: 11:00 am PT, 2:00 pm ET
Special Guests:
James Wilson, MD, PhD (Perelman School of Medicine, University of Pennsylvania)
Artur Padzik, PhD (AAV Production Manager, Biovian)
Gene therapy has made tremendous strides over the past decade or so. The first approved drugs are on the market, and literally hundreds of trials are underway offering unprecedented hope to patients with rare, debilitating genetic disorders. Nevertheless, safety issues continue to swirl around the field as adverse events are reported in trials involving both lentivirus and AAV vectors. Pricing and manufacturing pose additional hurdles that could significantly challenge the field.