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Kids with bubble boy disease could finally get access to gene therapy, as study starts back up at UCLA
While families who have kids with the disease are desperate for the therapy, drug companies have been uninterested because they can't make money.
United states
Donald kohn
Jakob kamil guziak
Soto abdul rahim
Paola andrea fern
David jensen
Kyler zeleny
University college london
Drug administration
California stem cell report
Andrea fern
Bubble Boy Disease Has a Cure, but Drug Companies Won t Provide It
Jakob, who was born with a rare illness, is 2 years old. But what's keeping him isolated from the world isn't his disease it's the marketplace.
United states
Stanford university
United kingdom
Matthew porteus
Donald kohn
Alessandro aiuti
Paola andrea fern
Manny lichtman
John travolta
Ceos andrea
Maria grazia roncarolo
David vetter
Emma walmsley
Jakob kamil guziak
Peter marks
Ethan perlstein
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