The researchers made the interesting finding using a trial involving patients with a rare genetic condition called Alpha-1 antitrypsin deficiency (AATD).
Parents of children with rare disease want clinical trials to save their children. Many become advocates. Even if they die, participating in research adds meaning.
Parents Of Kids With Rare Diseases Want Clinical Trials For Treatment today.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from today.com Daily Mail and Mail on Sunday newspapers.
Researchers have retrospectively analyzed data from nearly 60 patients with ocular myasthenia gravis (MG) not adequately responding to oral prednisone, finding that both intravenous (IV) methylprednisolone and tacrolimus monotherapy helped reduce symptoms.