/PRNewswire/ BioMarin Pharmaceutical Inc. (Nasdaq: BMRN) announced that positive new data supporting the safety and efficacy of VOXZOGO® (vosoritide) in.
The Anthony Nolan charity is celebrating 50 years since a mum’s love inspired the first stem cell register. Lizzie Catt speaks to three families about their hunt for incredible people willing to help their children
A survey of more than 60 families living with Noonan Syndrome has highlighted the need for more social support and medical awareness.
Noonan Syndrome, though c