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UCB announces U S FDA acceptance of new drug application and EMA MAA validation for zilucoplan for the treatment of generalized myasthenia gravis in adult patients

New drug application (NDA) for zilucoplan seeks approval for the treatment of generalized myasthenia gravis (gMG) in adult patients who are acetylcholine.

United kingdomBruxelles capitaleGreat britainDaphne teoCharl van zylJim baxterIris loew friedrichNeuromuscul disordAntje witteLaurent schotsUs communicationsBrand communicationsEu internationalEuropean commissionDrug administrationNeurology solutions head

Disease Modifying Therapies for Children with Spinal Atrophy

An update on the emerging evidence of the effects and safety of disease modifying therapies for the management of children with spinal muscular atrophy (SMA).

United statesNoord hollandNordrhein westfalenNat genetHansa biopharmaPetzolda neurofilamentClin neurophysiolSanofi genzymeThomas sejersenNeuromuscul disordPediatr pulmonolDement neuropsycholZetterbergh neurofilamentDunaway youngDhillons risdiplamWorld muscle society virtual congress

Dynacure Receives Fast Track Designation for DYN101, an Investigational Antisense Oligonucleotide for the Treatment of Myotubular and Centronuclear Myopathies

/PRNewswire/ Dynacure, a clinical stage biotechnology company focusing on Myotubular and Centronuclear Myopathies (CNM), a group of rare, debilitating, and.

United statesCentronuclear myopathiesPrnewswire dynacureNeuromuscul disordEuropean unionDrug administrationIonis pharmaceuticalsFast track designationFast trackLeen thielemansChief development officerHealth care amp hospitalsMedical pharmaceuticalsFda approval

Dynacure Receives Fast Track Designation for DYN101, an Investigational Antisense Oligonucleotide for the Treatment of Myotubular and Centronuclear Myopathies

/PRNewswire/ Dynacure, a clinical stage biotechnology company focusing on Myotubular and Centronuclear Myopathies (CNM), a group of rare, debilitating, and.

United statesCentronuclear myopathiesPrnewswire dynacureNeuromuscul disordEuropean unionDrug administrationIonis pharmaceuticalsFast track designationFast trackLeen thielemansChief development officer

Dynacure to Present Preclinical Data on Disease Progression Modelling and ASO-Mediated Dynamin 2 Knockdown at World Muscle Society (WMS) Meeting

Dynacure to Present Preclinical Data on Disease Progression Modelling and ASO-Mediated Dynamin 2 Knockdown at World Muscle Society (WMS) Meeting
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United statesCentronuclear myopathiesBelinda cowlingNeuromuscul disordEuropean unionEuropean medicines agencyWorld muscle societyIonis pharmaceuticalsAnnual congressChief scientific officer belinda cowlingInvestigational new drugIonis pharmaceuticalOrphan drugHereditary spastic paraplegiasஒன்றுபட்டது மாநிலங்களில்பெலிண்டா கோலிங்