Gene therapy for severe hemophilia is approved by FDA yoursourceone.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from yoursourceone.com Daily Mail and Mail on Sunday newspapers.
U.S. health regulators have approved a gene therapy for the most common form of hemophilia. The treatment, Roctavian, is an infusion that's been shown to reduce dangerous bleeding problems caused by the inherited condition. The Food and Drug Administration approved it Thursday for adult patients with severe cases of hemophilia A. That's the blood-clotting disorder that can lead to bleeding after minor injuries or scrapes. Drugmaker BioMarin said it will charge $2.9 million for the therapy. The therapy is a long-awaited alternative to current treatments. Those include weekly doses of a protein needed to help blood clot.
U.S. officials on Thursday approved drugmaker BioMarin's gene therapy for the most common form of hemophilia, an infused treatment that can significantly reduce dangerous bleeding problems.