After disappointing phase 3 trial results in ALS, Amylyx will pull Relyvrio from the market but provide it free to patients who want to stay on the medication.
Treatments for amyotrophic lateral sclerosis and paroxysmal nocturnal hemoglobinuria have been given marketing authorization by the European Medicines Agency.
The FDA has rejected Clene Nanomedicine's application for accelerated approval for the experimental drug ALS drug, CNM-Au8, citing insufficient evidence.
Federal health advisors voted 17-1 against an experimental treatment for Lou Gehrig's disease dubbed NurOwn, although the FDA is not bound by the vote.
The death of Bryan Randall, Sandra Bullock's longtime partner, brought new attention to ALS, also known as Lou Gehrig's disease, a devastating diagnosis affecting thousands of Americans.