Hemophilia can cause spontaneous and severe bleeding following an injury. Experts say gene therapies hold even more promise of one day curing the disease.
Canada: Pfizer said on Wednesday that Canada s health regulator approved its gene therapy for the treatment of a rare inherited bleeding disorder called hemophilia B ahead of a U.S. decision.The.
Education, psychological support, and implementation guidance are the top unmet needs identified by investigators from the United Kingdom concerning gene therapy use for hemophilia.