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Therapy to treat rare, hereditary diseases: Study
The study shows that gene therapy can help in treating rate and hereditary diseases, even the ones that affect just a handful people. | Health
Magnar bjoras
Department of clinical
Oslo university hospital
Norwegian university of science
Norwegian university
Middle east
Gene therapy
Gene therapy vectors
Stem cell gene therapy
Way to deliver clinically used gene therapy vectors
Gene therapy can treat rare diseases
Gene therapy can treat hereditary diseases
Way to deliver clinically used gene therapy vectors: Study
The study explored the safety and practicality of gene delivery to several brain regions with a noninvasive, ultrasound-based approach. | Health
Jerzy szablowski
Shirin nouraein
Laboratory for noninvasive neuroengineering
Targeted noninvasive gene therapy
Large brain volumes
Gene therapy
Stem cell gene therapy
Gene therapy vectors
Gene delivery
Noninvasive approach
Ultrasound based approach
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