A recent clinical trial, BRILLIANCE demonstrated the safety and efficacy of CRISPR gene editing in treating inherited blindness caused by mutations in the CEP290 gene.
BRILLIANCE trial results showed 11 out of 14 treated participants experienced some improvements in vision and quality of life measures.
CRISPR-based therapy
A recent clinical trial has shown promising results for a CRISPR/Cas9 gene editing therapy that could potentially restore vision in individuals with a rare type of inherited or congenital blindness.
Results from a groundbreaking clinical trial of CRISPR gene editing in 14 individuals with a form of inherited blindness show that the treatment is safe and led to measurable improvements in 11 of the participants treated.
Participants of pioneering CRISPR gene editin eurekalert.org - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from eurekalert.org Daily Mail and Mail on Sunday newspapers.