/PRNewswire/ Orsini Specialty Pharmacy, a leading independent specialty pharmacy focused on rare diseases and gene therapies, announced today that Krystal.
23.05.2023 - Company to Deliver to Patients FDA-Approved Topical Treatment for Dystrophic Epidermolysis Bullosa (DEB) Announces Collaboration with Amedisys to Administer Treatment in the Home BANNOCKBURN, Ill., May 23, 2023 (GLOBE NEWSWIRE) - Option Care .
The FDA on May 19 approved the first drug to treat patients with dystrophic epidermolysis bullosa a rare genetic disorder that causes fragile skin and persistent sores.
Krystal Biotech Receives FDA Approval for the First-Ever Redosable Gene Therapy, VYJUVEK™ (beremagene geperpavec-svdt) for the Treatment of Dystrophic Epidermolysis Bullosa streetinsider.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from streetinsider.com Daily Mail and Mail on Sunday newspapers.
Dystrophic Epidermolysis Bullosa (DEB) is a serious rare genetic disease that affects the skin and mucosal tissues and is caused by one or more mutations.