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A new drug for sickle cell disease appears to be effective in a mouse model of the condition. Now, a new study concludes that the drug is safe for humans.
Date Time
Toward a reliable oral treatment for sickle cell disease
Note to journalists: Please report that this research will be presented at a meeting of the American Chemical Society.
A press conference on this topic will be held Friday, April 9, at 10 a.m. Eastern time online at www.acs.org/acsspring2021conferences.
WASHINGTON, April 9, 2021 – For the millions of people worldwide who have sickle cell disease, there are only a few treatment options, which include risky bone marrow transplants, gene therapy or other treatments that address a subset of symptoms. Today, researchers will describe the discovery of a small molecule with the potential to address the root cause of sickle cell disease by boosting levels of fetal hemoglobin, a healthy form that adults normally do not make. The drug could be formulated into a convenient daily tablet.
Toward a reliable oral treatment for sickle cell disease eurekalert.org - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from eurekalert.org Daily Mail and Mail on Sunday newspapers.