Found in the river wyre close to where she disappeared. The mother of two was last seen walking her dog late last month. Now on bbc news, bittersweet medicine. This is a story of hope. How a new treatment is stopping a devastating genetic disease in its tracks. We have had almost nothing to offer families with this condition for decades. Bringing a new medicine to the world that can potentially cure these devastating diseases is incredibly satisfying and rewarding. How britains most expensive medicine is giving children their lives back. Its amazing. I mean, shes such a little character and for her to receive this treatment is just an absolute blessing. Theyre literally walking, running miracles, you know . They shouldnt be here. Im fergus walsh, the bbc s medical editor. Ive been following the first patient treated by the nhs with this life saving drug, and meeting families affected by one of the rarest and cruellest of genetic conditions. Nala, charlie, nala, charlie shaw. This is th
submitted a bid to buy manchester united bbc sport understands that a rival bid was also tabled by ineos. now it s time for bittersweet medicine. this is a story of hope. how a new treatment is stopping a devastating genetic disease in its tracks. we have had almost nothing to offer families with this condition for decades. bringing a new medicine to the world that can potentially cure these devastating diseases is incredibly satisfying and rewarding. how britain s most expensive medicine is giving children their lives back. it s amazing. i mean, she s such a little character and for her to receive this treatment is just an absolute blessing. they re literally walking, running miracles, you know? they shouldn t be here. i m fergus walsh, the bbc s medical editor. i ve been following the first patient treated by the nhs with this life saving drug, and meeting families affected by one of the rarest and cruellest of genetic conditions. # nala, charlie, nala, charlie shaw. th
found in the river wyre close to where she disappeared. the mother of two was last seen walking her dog late last month. now on bbc news, bittersweet medicine. this is a story of hope. how a new treatment is stopping a devastating genetic disease in its tracks. we have had almost nothing to offer families with this condition for decades. bringing a new medicine to the world that can potentially cure these devastating diseases is incredibly satisfying and rewarding. how britain s most expensive medicine is giving children their lives back. it s amazing. i mean, she s such a little character and for her to receive this treatment is just an absolute blessing. they re literally walking, running miracles, you know? they shouldn t be here. i m fergus walsh, the bbc s medical editor. i ve been following the first patient treated by the nhs with this life saving drug, and meeting families affected by one of the rarest and cruellest of genetic conditions. # nala, charlie, nala, char
we have the ability to offer potentially curative therapies, and we are letting our children down by not screening for these conditions because those devastating conditions are so preventable if you can identify them at birth, and then offer these kinds of innovative therapies. as forjake and allie shaw, they don t yet know how much time they ll have with nala whether it s months or years. sing-song: nala charlie shaw. one thing they re certain of is wanting to ensure other families are spared what they re going through. it s too late for our child, but i would like to think that if another child was born, it could be picked up quick enough for them to be saved. i just want to get as much awareness out there as possible and i thinkif there s the more awareness we have and the more people pushing for it to be put on the blood spot test, then it s a good place to start, isn t it?
potentially curative therapies, and we are letting our children down by not screening for these conditions because those devastating conditions are so preventable if you can identify them at birth, and then offer these kinds of innovative therapies. as forjake and allie shaw, they don t yet know how much time they ll have with nala whether it s months or years. one thing they re certain of is wanting to ensure other families are spared what they re going through. it s too late for our child, but i would like to think that if another child was born, it could be picked up quick enough for them to be saved. ijust want to get as much awareness out there as possible, and i think the more awareness we have and the more people pushing for it to be put on the blood spot test, then it s a good place to start, isn t it? years, we spent not knowing