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Devastating genetic disease in children may be treatable in adulthood
A devastating genetic disease called CDKL5 deficiency disorder (CDD), which strikes in early childhood, may be significantly treatable even in adulthood, a new study from the Perelman School of Medicine at the University of Pennsylvania suggests.
Barbara-terzic
Zhaolan-joe-zhou
Marc-fuccillo
Felicia-davatolhagh
Emily-henderson
University-of-pennsylvania
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Perelman-school
Clinical-investigation
Senior-author
Cdkl5
Enetic
Penn Study Suggests Genetic Disease CDKL5 Deficiency Disorder Could Be Treatable after Childhood
PHILADELPHIA A devastating genetic disease called CDKL5 deficiency disorder (CDD), which strikes in early childhood, may be significantly treatable
University-of-pennsylvania
Pennsylvania
United-states
Philadelphia
Barbara-terzic
Zhaolan-joe-zhou
Marc-fuccillo
Felicia-davatolhagh
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Loulou-foundation
Perelman-school-of-medicine
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