AIDS virus used in gene therapy to fix bubble baby disease
MARILYNN MARCHIONE, AP Chief Medical Writer
May 11, 2021
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1of3This January 2020 photo provided by the family shows Josselyn Kish of Las Vegas. As a baby, Josselyn suffered rashes, painful shingles and frequent diarrhea, said her mother, Kim Carter. “Day care was calling me a couple times a week to come get her because she was always getting fevers.” After the gene therapy, “she was better right away,” Carter said. Now, “she rarely, rarely gets sick at all” and has been able to recover whenever she has. (Family photo via AP)Kim Carter/APShow MoreShow Less
Factor Bioscience to Deliver Six Digital Presentations at the American Society of Gene & Cell Therapy (ASGCT) 24th Annual Meeting
-The presentations will reveal advances in mRNA, circleRNA, gene editing, cell reprogramming, and iPS cell-derived NK-cell technologies.
- Factor s participation in this year s ASGCT Annual Meeting marks the company s ten-year anniversary and represents the most comprehensive presentation of the company s data to date.
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CAMBRIDGE, Mass., May 11, 2021 /PRNewswire/ Factor Bioscience Inc., a Cambridge-based biotechnology company focused on developing mRNA and cell-engineering technologies, announced its participation in the American Society of Gene & Cell Therapy (ASGCT) 24th Annual Meeting to be held virtually May 11-14, 2021, at which Factor will deliver six digital presentations:
Marilynn Marchione
This January 2020 photo provided by the family shows Josselyn Kish of Las Vegas. As a baby, Josselyn suffered rashes, painful shingles and frequent diarrhea, said her mother, Kim Carter. âÄúDay care was calling me a couple times a week to come get her because she was always getting fevers.âÄù After the gene therapy, âÄúshe was better right away,âÄù Carter said. Now, âÄúshe rarely, rarely gets sick at allâÄù and has been able to recover whenever she has. (Family photo via AP) May 11, 2021 - 3:01 AM
A gene therapy that makes use of an unlikely helper, the AIDS virus, gave a working immune system to 48 babies and toddlers who were born without one, doctors reported Tuesday.
An experimental gene therapy that makes use of an unlikely helper, the AIDS virus, has successfully treated 48 out of 50 children who were born without an immune system due to a deadly disorder, a new study shows.
Such results were published on Tuesday by the New England Journal of Medicine and presented at an online American Society of Gene & Cell Therapy conference.
All but two of the 50 children who were given the experimental therapy as part of the study now have healthy germ-fighting abilities.
“We’re taking what otherwise would have been a fatal disease” and healing most of these children with a single treatment, study leader Donald Kohn of UCLA Mattel Children’s Hospital, told the Associated Press news agency.
This January 2020 photo provided by the family shows Josselyn Kish of Las Vegas. As a baby, Josselyn suffered rashes, painful shingles and frequent diarrhea, said her mother, Kim Carter. (Family photo via AP)
(AP) A gene therapy that makes use of an unlikely helper, the AIDS virus, gave a working immune system to 48 babies and toddlers who were born without one, doctors reported Tuesday.
Results show that all but two of the 50 children who were given the experimental therapy in a study now have healthy germ-fighting abilities.
“We’re taking what otherwise would have been a fatal disease” and healing most of these children with a single treatment, said study leader Dr. Donald Kohn of UCLA Mattel Children’s Hospital.