Gene therapy can provide long-lasting therapeutic benefit in Huntington's disease

Gene therapy targeting the messenger RNA (mRNA) of the mutated huntingtin gene (HTT) can provide long-lasting therapeutic benefit in Huntington's disease after a single administration.

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Terencer Flotte ,Emily Henderson ,Dinah Sah , ,Human Gene ,Voyager Therapeutics ,Gene ,Gene Therapy ,Huntington 39s Disease ,N Vivo ,Na ,Herapeutics ,