First gene therapy approach for MLC leukoencephalopathy designated as orphan drug

The European Medicines Agency (EMA) has designated as an orphan drug the first gene therapy approach to treat megalencephalic leukoencephalopathy with

Related Keywords

Hebron ,Israel General ,Israel , ,Biomedical Research Network On Rare Diseases ,Catalan Institution For Research ,Department Of Physiological Sciences ,European Medicines Agency ,Institute Of Neurosciences ,Hebron Research Institute ,Subcortical Cysts ,Physiological Sciences ,Biomedical Research Network ,Rare Diseases ,Gene Therapy ,Catalan Institution ,Advanced Studies ,