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Juliana Biondo, MD: Bispecific mAbs and FVIII Gene Therapy for Hemophilia A

Dr. Juliana Biondo discusses the exciting FDA approval of Roctavian and how it compares with other treatment options like Hemlibra.

Executive Branch Latest News And Press Releases June 30,2023

SEC Charges Former Pfizer Statistician with Insider Trading Ahead of COVID-19 Announcement. CBP officers seize nearly 900,000 fentanyl pills in California Event

U.S. Food and Drug Administration Approves BioMarin's ROCTAVIAN™ (valoctocogene roxaparvovec-rvox), the First and Only Gene Therapy for Adults with Severe Hemophilia A

/PRNewswire/ BioMarin Pharmaceutical Inc. (Nasdaq: BMRN), a global biotechnology company dedicated to transforming lives through genetic discovery, today.

Roctavian Receives Approval by the FDA for Severe Hemophilia A

The approval is supported by positive results from the largest and longest phase 3 study for gene therapy in hemophilia, showing a 52% reduction in annualized bleeding rate compared with baseline rates on routine prophylaxis.

U.S. Food and Drug Administration Approves BioMarin's ROCTAVIAN™ (valoctocogene roxaparvovec-rvox), the First and Only Gene Therapy for Adults with Severe…