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Cipaglucosidase/Miglustat for Pompe Disease: The Long-Term Safety, Efficacy

Treatment with cipaglucosidase/miglustat up to 104 weeks is safe and effective for ambulatory patients with late-onset Pompe disease.

Phoenix
Arizona
United-states
American-association-of-neuromuscular-electrodiagnostic-medicine
Electrodiagnostic-medicine
Annual-meeting

How Do Neuromuscular Diseases Affect Prevalence of Neuropsychiatric Conditions?

The presence of neuropsychiatric conditions, such as depression, is more prevalent among patients with neuromuscular diseases.

Arizona
United-states
Phoenix
National-inpatient-sample
American-association-of-neuromuscular-electrodiagnostic-medicine
Electrodiagnostic-medicine
Annual-meeting

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