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BridgeBio Bounces Back with Promising Canavan, MD Data

After suffering a blow to its multi-billion dollar liver cancer program, BridgeBio presented early but promising data in ultra-rare Canavan disease.

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BridgeBio Pharma Inc. (BBIO) Presents Updated Positive Data from its BBP-812 Canavan Disease Gene Therapy Program

BridgeBio Pharma Inc. (BBIO) Presents Updated Positive Data from its BBP-812 Canavan Disease Gene Therapy Program
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Dr. Michael V. Johnston, former chief medical officer and executive vice president at Kennedy Krieger Institute, dies

Dr. Michael V. Johnston, former chief medical officer and executive vice president at the Kennedy Krieger Institute who enjoyed sailing summers in Maine, died July 30.

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Budget Amendment Removes Parental Consent for Preventive Care

/PRNewswire/ The Coalition for Parental Choice today urged Governor Charlie Baker to veto a budget amendment which would remove parental consent for.

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Upstaza™ Granted Marketing Authorization by European Commission as First Disease-Modifying Treatment for AADC Deficiency

Upstaza™ Granted Marketing Authorization by European Commission as First Disease-Modifying Treatment for AADC Deficiency
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