Interview: The processes and difficulties of working within rare diseases

OSP was delighted to speak to Galina Nesterova, executive medical director at the Rare Disease & Pediatrics Center of Excellence, and Susan McKune, vice president of pediatrics and clinical pharmacology both within medical science and strategy at PPD, part of Thermo Fisher. They answered some pertinent questions surrounding rare diseases.

Related Keywords

,Cpath Rare Disease Clinical Outcome Assessment Consortium ,International Rare Diseases Research Consortium Irdi ,International Rare Diseases Research Consortium ,Breakthrough Therapy ,Fast Track ,Orphan Drug Designation ,Prescription Drug User Fee ,Rare Pediatric Diseases ,Priority Review Voucher ,Both Center ,Drug Evaluation ,Biologics Evaluation ,Rare Disease ,Preclinical Research ,Clinical Development ,Atient Centricity ,Regulations ,Contract Manufacturing ,Data Management ,Thermo Fisher ,Thermo Fisher Scientific ,Research ,Clinical Trials ,